(Q42674306)
Statements
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Effect of enzyme therapy in juvenile patients with Pompe disease: a three-year open-label study (English)
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C I van Capelle
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N A M E van der Beek
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M L C Hagemans
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W F M Arts
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W C J Hop
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P Lee
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J Jaeken
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I M E Frohn-Mulder
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P J F M Merkus
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D Corzo
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A C Puga
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A J Reuser
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A T van der Ploeg
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1 December 2010
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20
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12
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775-782
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Identifiers
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