(Q45870746)

English

Ex vivo gene therapy using bone marrow-derived cells: combined effects of intracerebral and intravenous transplantation in a mouse model of Niemann-Pick disease

scientific article published in December 2003

In more languages

Statements

scholarly article

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

Ex vivo gene therapy using bone marrow-derived cells: combined effects of intracerebral and intravenous transplantation in a mouse model of Niemann-Pick disease (English)

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

0 references

Edward H Schuchman

2

object named as

Edward H Schuchman

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

author name string

Hee-Kyung Jin

1

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

publication date

1 December 2003

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

Molecular Therapy

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

8

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

6

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

876-885

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

Niemann-Pick disease (variation in the sphingomyelinase deficient group). Neurovisceral phenotype (A) with an abnormally protracted clinical course and variable expression of neurological symptomatology in three siblings.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Acid sphingomyelinase deficient mice: a model of types A and B Niemann-Pick disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Acid sphingomyelinase-deficient mice mimic the neurovisceral form of human lysosomal storage disease (Niemann-Pick disease)

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Replacement Therapy for Inherited Enzyme Deficiency

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Enzyme therapy in Fabry disease: differential in vivo plasma clearance and metabolic effectiveness of plasma and splenic alpha-galactosidase A isozymes

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Phosphohexosyl components of a lysosomal enzyme are recognized by pinocytosis receptors on human fibroblasts

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Lysosomal enzyme transfer from different types of lymphoid cell

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Fluorescence-Based Selection of Retrovirally Transduced Cells in the Absence of a Marker Gene: Direct Selection of Transduced Type B Niemann-Pick Disease Cells and Evidence for Bystander Correction

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Donor-derived cells in the central nervous system of twitcher mice after bone marrow transplantation

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Bone marrow transplantation corrects the enzyme defect in neurons of the central nervous system in a lysosomal storage disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Hematopoietic stem cell gene therapy leads to marked visceral organ improvements and a delayed onset of neurological abnormalities in the acid sphingomyelinase deficient mouse model of Niemann-Pick disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Functional amelioration of murine galactosialidosis by genetically modified bone marrow hematopoietic progenitor cells

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Neural progenitor cell engraftment corrects lysosomal storage throughout the MPS VII mouse brain

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Engraftment of genetically engineered amniotic epithelial cells corrects lysosomal storage in multiple areas of the brain in mucopolysaccharidosis type VII mice

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Neuronal progenitor cells of the neonatal subventricular zone differentiate and disperse following transplantation into the adult rat striatum.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Long-term survival of human central nervous system progenitor cells transplanted into a rat model of Parkinson's disease.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Migration patterns and phenotypic differentiation of long-term expanded human neural progenitor cells after transplantation into the adult rat brain

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Engraftment and migration of human bone marrow stromal cells implanted in the brains of albino rats--similarities to astrocyte grafts

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Marrow stromal cells migrate throughout forebrain and cerebellum, and they differentiate into astrocytes after injection into neonatal mouse brains

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Multipotential marrow stromal cells transduced to produce L-DOPA: engraftment in a rat model of Parkinson disease

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Intracerebral transplantation of mesenchymal stem cells into acid sphingomyelinase-deficient mice delays the onset of neurological abnormalities and extends their life span.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Biochemical, pathological, and clinical response to transplantation of normal bone marrow cells into acid sphingomyelinase-deficient mice

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Infusion of recombinant human acid sphingomyelinase into niemann-pick disease mice leads to visceral, but not neurological, correction of the pathophysiology

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Neogenesis of cerebellar Purkinje neurons from gene-marked bone marrow cells in vivo.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Contribution of transplanted bone marrow cells to Purkinje neurons in human adult brains

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Behavior of human neural progenitor cells transplanted to rat brain

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Arylsulfatase B activities and glycosaminoglycan levels in retrovirally transduced mucopolysaccharidosis type VI cells. Prospects for gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Retrovirus-mediated transfer of the human alpha-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Packaging cell line DNA contamination of vector supernatants: implication for laboratory and clinical research

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Lysenin, a novel sphingomyelin-specific binding protein

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Characterization of human acid sphingomyelinase purified from the media of overexpressing Chinese hamster ovary cells

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

The quantiative measurement of motor inco-ordination in naive mice using an acelerating rotarod

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

Differentiation and angiogenesis of central nervous system stem cells implanted with mesenchyme into ischemic rat brain

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

based on heuristic

inferred from DOI database lookup

A safe packaging line for gene transfer: separating viral genes on two different plasmids

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.008

7 January 2021

based on heuristic

inferred from DOI database lookup

Identifiers

10.1016/J.YMTHE.2003.07.008

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

PubMed publication ID

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/14664789

ResearchGate publication ID

0 references

Sitelinks

Wikipedia(0 entries)

Wikibooks(0 entries)

Wikinews(0 entries)

Wikiquote(0 entries)

Wikisource(0 entries)

Wikiversity(0 entries)

Wikivoyage(0 entries)

Wiktionary(0 entries)

Multilingual sites(0 entries)

Retrieved from "https://www.wikidata.org/w/index.php?title=Q45870746&oldid=2087728018"