(Q45872026)

17 December 2017

title

Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats (English)

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17 December 2017

author name string

J Hordeaux

1

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17 December 2017

L Dubreil

2

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17 December 2017

J Deniaud

3

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17 December 2017

F Iacobelli

4

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17 December 2017

S Moreau

5

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17 December 2017

M Ledevin

6

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17 December 2017

C Le Guiner

7

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17 December 2017

V Blouin

8

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17 December 2017

J Le Duff

9

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17 December 2017

A Mendes-Madeira

10

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17 December 2017

F Rolling

11

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17 December 2017

Y Cherel

12

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17 December 2017

P Moullier

13

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17 December 2017

M-A Colle

14

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17 December 2017

publication date

15 January 2015

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17 December 2017

published in

Gene Therapy

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17 December 2017

volume

22

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17 December 2017

issue

4

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17 December 2017

page(s)

316-324

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17 December 2017

Gene therapy for lysosomal storage diseases (LSDs) in large animal models

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Expansive Gene Transfer in the Rat CNS Rapidly Produces Amyotrophic Lateral Sclerosis Relevant Sequelae When TDP-43 is Overexpressed

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RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy

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Several rAAV vectors efficiently cross the blood-brain barrier and transduce neurons and astrocytes in the neonatal mouse central nervous system

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Widespread spinal cord transduction by intrathecal injection of rAAV delivers efficacious RNAi therapy for amyotrophic lateral sclerosis

21 January 2018

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21 January 2018

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21 January 2018

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Adeno-associated virus of a single-polarity DNA genome is capable of transduction in vivo

21 January 2018

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21 January 2018

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21 January 2018

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https://api.crossref.org/works/10.1038%2FGT.2014.121

21 January 2018

Identifiers

DOI

10.1038/GT.2014.121

1 reference

17 December 2017

Dimensions Publication ID

1009724714

0 references

1 reference

17 December 2017