(Q45882673)

17 December 2017

title

Prospects for gene therapy of inherited retinal disease (English)

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17 December 2017

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17 December 2017

publication date

16 January 2009

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17 December 2017

published in

Eye

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17 December 2017

volume

23

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17 December 2017

issue

10

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17 December 2017

page(s)

1898-1903

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17 December 2017

Molecular genetics and prospects for therapy of the inherited retinal dystrophies

cites work

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Electrically assisted ocular gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Co-injection of adenovirus expressing CTLA4-Ig prolongs adenovirally mediated lacZ reporter gene expression in the mouse retina.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Immune responses limit adenovirally mediated gene expression in the adult mouse eye.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Barriers for retinal gene therapy: separating fact from fiction

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Gene transfer into the mouse retina mediated by an adeno-associated viral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Infection with adeno-associated virus may protect against excitotoxicity.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Recombinant adeno-associated virus serotype 4 mediates unique and exclusive long-term transduction of retinal pigmented epithelium in rat, dog, and nonhuman primate after subretinal delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Versatility of AAV vectors for retinal gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Novel AAV serotypes for improved ocular gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

AAV-mediated gene therapy for retinal disorders: from mouse to man.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Stable rAAV-mediated transduction of rod and cone photoreceptors in the canine retina

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Gene transfer to the nonhuman primate retina with recombinant feline immunodeficiency virus vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Stable and efficient intraocular gene transfer using pseudotyped EIAV lentiviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Correction of the disease phenotype in the mouse model of Stargardt disease by lentiviral gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Activity analysis of housekeeping promoters using self-inactivating lentiviral vector delivery into the mouse retina.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Lentiviral vector-mediated gene transfer in adult mouse photoreceptors is impaired by the presence of a physical barrier

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Gene replacement therapy rescues photoreceptor degeneration in a murine model of Leber congenital amaurosis lacking RPGRIP.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

RS-1 Gene Delivery to an Adult Rs1h Knockout Mouse Model Restores ERG b-Wave with Reversal of the Electronegative Waveform of X-Linked Retinoschisis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Retinoschisin gene therapy and natural history in the Rs1h-KO mouse: long-term rescue from retinal degeneration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

AAV-Mediated gene transfer slows photoreceptor loss in the RCS rat model of retinitis pigmentosa

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Lack of fundus autofluorescence to 488 nanometers from childhood on in patients with early-onset severe retinal dystrophy associated with mutations in RPE65.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Functional and structural recovery of the retina after gene therapy in the RPE65 null mutation dog.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Effect of gene therapy on visual function in Leber's congenital amaurosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Safety and efficacy of gene transfer for Leber's congenital amaurosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

RNA interference-mediated suppression and replacement of human rhodopsin in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2Rd2/Rd2 model of retinal degeneration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

In contrast to AAV-mediated Cntf expression, AAV-mediated Gdnf expression enhances gene replacement therapy in rodent models of retinal degeneration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FEYE.2008.412

21 January 2018

Identifiers

DOI

10.1038/EYE.2008.412

1 reference

17 December 2017

Dimensions Publication ID

1019062955

0 references

1 reference

17 December 2017