(Q45883135)

17 December 2017

title

Lessons learned from the gene therapy trial for ornithine transcarbamylase deficiency (English)

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17 December 2017

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James M Wilson

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17 December 2017

publication date

10 February 2009

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17 December 2017

Molecular Genetics and Metabolism

published in

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17 December 2017

volume

96

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17 December 2017

issue

4

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17 December 2017

page(s)

151-157

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17 December 2017

Ornithine carbamoyltransferase deficiency

cites work

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

The role of orthotopic liver transplantation in the treatment of ornithine transcarbamylase deficiency.

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Amino Acid Acylation: A Mechanism of Nitrogen Excretion in Inborn Errors of Urea Synthesis

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Prolonged metabolic correction in adult ornithine transcarbamylase-deficient mice with adenoviral vectors

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Adenovirus-mediated in vivo gene transfer rapidly protects ornithine transcarbamylase-deficient mice from an ammonium challenge

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Gene transfer into the liver of nonhuman primates with E1-deleted recombinant adenoviral vectors: safety of readministration

7 January 2021

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MHC class I-restricted cytotoxic T lymphocytes to viral antigens destroy hepatocytes in mice infected with E1-deleted recombinant adenoviruses.

7 January 2021

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7 January 2021

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A pilot study of in vivo liver-directed gene transfer with an adenoviral vector in partial ornithine transcarbamylase deficiency

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

En route to ethical recommendations for gene transfer clinical trials

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer

7 January 2021

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Activation of innate immunity in nonhuman primates following intraportal administration of adenoviral vectors.

7 January 2021

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Acute cytokine response to systemic adenoviral vectors in mice is mediated by dendritic cells and macrophages

7 January 2021

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Evaluation of toxicity from high-dose systemic administration of recombinant adenovirus vector in vector-naive and pre-immunized mice.

7 January 2021

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Preexisting immunity to adenovirus in rhesus monkeys fails to prevent vector-induced toxicity

7 January 2021

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Protecting research subjects--what must be done

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Everyone's a little bit biased (even physicians).

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

Readability standards for informed-consent forms as compared with actual readability

7 January 2021

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End-stage heart disease, high-risk research, and competence to consent: the case of the AbioCor artificial heart

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2008.12.016

10.1016/J.YMGME.2008.12.016

7 January 2021

Identifiers

DOI

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17 December 2017

PubMed ID

19211285

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17 December 2017