(Q51837409)

13 April 2018

title

Induction of tolerance to a recombinant human enzyme, acid alpha-glucosidase, in enzyme deficient knockout mice (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12739885

1 January 2024

0 references

1 reference

10.1023/A:1022998010833

https://api.crossref.org/works/10.1023/A:1022998010833

1 January 2024

1 reference

10.1023/A:1022998010833

https://api.crossref.org/works/10.1023/A:1022998010833

1 January 2024

2

Kanneboyina Nagaraju

1 reference

13 April 2018

John Hopwood

7

object named as

John J Hopwood

1 reference

13 April 2018

author name string

Nina Raben

1

1 reference

13 April 2018

Alicia Lee

3

1 reference

13 April 2018

Nina Lu

4

1 reference

13 April 2018

Yesenia Rivera

5

1 reference

13 April 2018

Tejas Jatkar

6

1 reference

13 April 2018

John J. Hopwood

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12739885

1 January 2024

Paul H. Plotz

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12739885

1 January 2024

language of work or name

English

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=12739885

1 January 2024

publication date

1 April 2003

1 reference

13 April 2018

published in

Transgenic Research

1 reference

13 April 2018

volume

12

1 reference

13 April 2018

issue

2

1 reference

13 April 2018

page(s)

171-178

1 reference

13 April 2018

https://scigraph.springernature.com/pub.10.1023/a:1022998010833

exact match

0 references

cites work

Long-term and high-dose trials of enzyme replacement therapy in the canine model of mucopolysaccharidosis I.

1 reference

12 December 2020

Correction of the enzymatic and functional deficits in a model of Pompe disease using adeno-associated virus vectors

1 reference

12 December 2020

Determination of acid alpha-glucosidase protein: evaluation as a screening marker for Pompe disease and other lysosomal storage disorders

1 reference

12 December 2020

Generalized glycogen storage and cardiomegaly in a knockout mouse model of Pompe disease

1 reference

12 December 2020

Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

1 reference

12 December 2020

Glycogen stored in skeletal but not in cardiac muscle in acid alpha-glucosidase mutant (Pompe) mice is highly resistant to transgene-encoded human enzyme

1 reference

12 December 2020

Immune response to enzyme replacement therapy in lysosomal storage disorder patients and animal models.

1 reference

12 December 2020

Enzyme therapy for pompe disease with recombinant human alpha-glucosidase from rabbit milk

1 reference

12 December 2020

Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

1 reference

12 December 2020

Intercellular transfer of the virally derived precursor form of acid alpha-glucosidase corrects the enzyme deficiency in inherited cardioskeletal myopathy Pompe disease

1 reference

12 December 2020

Acid alpha-glucosidase deficiency (glycogenosis type II, Pompe disease).

1 reference

12 December 2020

Modulation of disease severity in mice with targeted disruption of the acid alpha-glucosidase gene

1 reference

12 December 2020

Myoblast gene therapy in canine mucopolysaccharidosis. I: Abrogation by an immune response to alpha-L-iduronidase

1 reference

12 December 2020

Recombinant human alpha-glucosidase from rabbit milk in Pompe patients.

1 reference

12 December 2020

lacZ transgenic rats tolerant for beta-galactosidase: recipients for gene transfer studies using lacZ as a reporter gene

1 reference

12 December 2020

Clinical and metabolic correction of pompe disease by enzyme therapy in acid maltase-deficient quail

1 reference

12 December 2020

Inhibitor antibody development and T cell response to human factor VIII in murine hemophilia A.

1 reference

12 December 2020

Induction of self-tolerance in T cells but not B cells of transgenic mice expressing little self antigen.

1 reference

12 December 2020

Long-term efficacy after [E1-, polymerase-] adenovirus-mediated transfer of human acid-alpha-glucosidase gene into glycogen storage disease type II knockout mice

1 reference

12 December 2020

Targeted disruption of the acid alpha-glucosidase gene in mice causes an illness with critical features of both infantile and adult human glycogen storage disease type II

1 reference

12 December 2020

Conditional tissue-specific expression of the acid alpha-glucosidase (GAA) gene in the GAA knockout mice: implications for therapy

1 reference

12 December 2020

Advances in hepatocyte transplantation: a myth becomes reality

1 reference

12 December 2020

Treatment of the Crigler-Najjar syndrome type I with hepatocyte transplantation

1 reference

12 December 2020

Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial

1 reference

12 December 2020

Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A

1 reference

12 December 2020

Human acid alpha-glucosidase from rabbit milk has therapeutic effect in mice with glycogen storage disease type II

1 reference

12 December 2020

Presence of hematopoietic stem cells in the adult liver

1 reference

12 December 2020

Biochemical, immunological, and cell genetic studies in glycogenosis type II

1 reference

12 December 2020

Active site mutant transgene confers tolerance to human beta-glucuronidase without affecting the phenotype of MPS VII mice.

1 reference

12 December 2020

Recombinant human acid alpha-glucosidase: high level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice

1 reference

12 December 2020

Muscle as a putative producer of acid alpha-glucosidase for glycogenosis type II gene therapy

1 reference

12 December 2020

Transgenic mouse lines that are immunologically tolerant and nontolerant to herpes simplex virus glycoprotein D

1 reference

12 December 2020

Correction of glycogen storage disease type II by enzyme replacement with a recombinant human acid maltase produced by over-expression in a CHO-DHFR(neg) cell line

1 reference

12 December 2020

Introduction of a xenogeneic gene via hematopoietic stem cells leads to specific tolerance in a rhesus monkey model

1 reference

12 December 2020

Identifiers

DOI

10.1023/A:1022998010833

1 reference

13 April 2018

Dimensions Publication ID

0 references

1 reference

13 April 2018