(Q30335768)

19 June 2017

1 reference

title

Taking the good out of the bad: lentiviral-based gene therapy of the hemoglobinopathies (English)

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

11 March 2024

0 references

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

11 March 2024

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

Applied Microbiology and Biotechnology

11 March 2024

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

11 March 2024

1

Peter B. Stathopulos

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14499152

11 March 2024

language of work or name

English

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=14499152

11 March 2024

publication date

1 September 2003

1 reference

full work available at URL

19 June 2017

https://api.elsevier.com/content/article/PII:S0734975003001022?httpAccept=text/xml

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

https://api.elsevier.com/content/article/PII:S0734975003001022?httpAccept=text/plain

11 March 2024

1 reference

https://api.crossref.org/works/10.1016/S0734-9750(03)00102-2

11 March 2024

published in

Biotechnology Advances

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19 June 2017

21

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19 June 2017

6

1 reference

19 June 2017

513-526

1 reference

Prospects for Human Gene Therapy

19 June 2017

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Isolation of a T-Lymphotropic Retrovirus from a Patient at Risk for Acquired Immune Deficiency Syndrome (AIDS)

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Ligand-induced conformational dependence of hemoglobin in sickling interactions

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Current developments in the design of onco-retrovirus and lentivirus vector systems for hematopoietic cell gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Transfer of genes to humans: early lessons and obstacles to success

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Lineage-specific expression of a human beta-globin gene in murine bone marrow transplant recipients reconstituted with retrovirus-transduced stem cells

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

[26] Generation of HIV-1 derived lentiviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Chromatin structure and transcriptional regulation of the beta-globin locus.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Historical essay. The early years of HIV/AIDS.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Position-independent, high-level expression of the human beta-globin gene in transgenic mice

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Gene mutations in human haemoglobin: the chemical difference between normal and sickle cell haemoglobin

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Expression of the human beta-globin gene following retroviral-mediated transfer into multipotential hematopoietic progenitors of mice

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Developmental regulation of human globin genes

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

A controlled study of adenoviral-vector-mediated gene transfer in the nasal epithelium of patients with cystic fibrosis

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Somatic spectrum of cancer-associated single basepair substitutions in the TP53 gene is determined mainly by endogenous mechanisms of mutation and by selection

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Mutagenesis of retroviral vectors transducing human beta-globin gene and beta-globin locus control region derivatives results in stable transmission of an active transcriptional structure

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Passage through mitosis is required for oncoretroviruses but not for the human immunodeficiency virus

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

5-Azacytidine Selectively Increases γ-Globin Synthesis in a Patient with β+Thalassemia

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Bone marrow transplantation in patients with thalassemia

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Successful treatment of murine beta-thalassemia intermedia by transfer of the human beta-globin gene

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Development of a self-inactivating lentivirus vector.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

The panoply of animal models for sickle cell anaemia

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Structural bases of the inhibitory effects of hemoglobin F and hemoglobin A2 on the polymerization of hemoglobin S

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

1 reference

7 January 2021

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

The beta-thalassemias

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Transgenic knockout mice with exclusively human sickle hemoglobin and sickle cell disease

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Correction of sickle cell disease in transgenic mouse models by gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Molecular Pathology of Human Haemoglobin

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Development of multigene and regulated lentivirus vectors

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Generation of a high-titer retroviral vector capable of expressing high levels of the human beta-globin gene

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

The immunopathogenesis of equine infectious anemia virus

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

HIV accessory proteins: leading roles for the supporting cast.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

High-level expression of hemoglobin A in human thalassemic erythroid progenitor cells following lentiviral vector delivery of an antisense snRNA.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Thalassemia--a global public health problem

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Crystal structure of sickle-cell deoxyhemoglobin at 5 A resolution.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

A mouse model for beta 0-thalassemia

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

HTLV-III in Cells Cultured from Semen of Two Patients with AIDS

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors.

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

A third-generation lentivirus vector with a conditional packaging system

1 reference

https://api.crossref.org/works/10.1016%2FS0734-9750%2803%2900102-2

7 January 2021

Identifiers

1 reference

19 June 2017

1 reference