(Q34629805)

3 August 2017

title

The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: lessons learned from infantile Pompe disease (English)

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3 August 2017

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9

Priya S Kishnani

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3 August 2017

Suhrad G Banugaria

1

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3 August 2017

Sean N Prater

2

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3 August 2017

Yiu-Ki Ng

3

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3 August 2017

Joyce A Kobori

4

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3 August 2017

Richard S Finkel

5

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3 August 2017

Roger L Ladda

6

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3 August 2017

Yuan-Tsong Chen

7

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3 August 2017

Amy S Rosenberg

8

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3 August 2017

language of work or name

English

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publication date

1 August 2011

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3 August 2017

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3 August 2017

volume

13

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3 August 2017

issue

8

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3 August 2017

page(s)

729-736

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A randomized study of alglucosidase alfa in late-onset Pompe's disease

3 August 2017

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

How we treat a hemophilia A patient with a factor VIII inhibitor

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Immune tolerance improves the efficacy of enzyme replacement therapy in canine mucopolysaccharidosis I.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Advances in hemophilia: experimental aspects and therapy

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Enhanced response to enzyme replacement therapy in Pompe disease after the induction of immune tolerance

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Deconstructing Pompe disease by analyzing single muscle fibers: to see a world in a grain of sand...

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Chinese hamster ovary cell-derived recombinant human acid alpha-glucosidase in infantile-onset Pompe disease

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

The natural course of infantile Pompe's disease: 20 original cases compared with 133 cases from the literature

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Human immune response to recombinant human proteins

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Left ventricular myocardial mass determined by cross-sectional echocardiography in normal newborns, infants, and children

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Pre- and postnatal pathology, enzyme treatment, and unresolved issues in five lysosomal disorders

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease

7 July 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Safety and efficacy of recombinant acid alpha-glucosidase (rhGAA) in patients with classical infantile Pompe disease: results of a phase II clinical trial

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Analysis of a glucose tetrasaccharide elevated in Pompe disease by stable isotope dilution–electrospray ionization tandem mass spectrometry

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Nonparametric Estimation from Incomplete Observations

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Induction of tolerance to a recombinant human enzyme, acid alpha-glucosidase, in enzyme deficient knockout mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Elimination of antibodies to recombinant enzyme in Pompe's disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Treatment of Fabry disease with different dosing regimens of agalsidase: effects on antibody formation and GL-3.

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Enzyme-replacement therapy in mucopolysaccharidosis I.

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Antibodies against rHuEPO: native and recombinant

21 January 2018

1 reference

https://api.crossref.org/works/10.1097%2FGIM.0B013E3182174703

Development of insulin antibodies, metabolic control and B-cell function in newly diagnosed insulin dependent diabetic children treated with monocomponent human insulin or monocomponent porcine insulin

21 January 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3954622

Enzyme replacement therapy in mucopolysaccharidosis I: altered distribution and targeting of alpha-L-iduronidase in immunized rats

26 October 2018

1 reference

12 December 2020

Liquid chromatographic assay for a glucose tetrasaccharide, a putative biomarker for the diagnosis of Pompe disease

1 reference

12 December 2020

Comparative study of biosynthetic human growth hormone immunogenicity in growth hormone deficient children

1 reference

12 December 2020

Antibody response in patients with Gaucher disease after repeated infusion with macrophage-targeted glucocerebrosidase

1 reference

12 December 2020

Incidence and significance of neutralizing antibodies to interferon beta-1a in multiple sclerosis. Multiple Sclerosis Collaborative Research Group (MSCRG)

1 reference

12 December 2020

Differential muscular glycogen clearance after enzyme replacement therapy in a mouse model of Pompe disease

1 reference

12 December 2020

Immune response to enzyme replacement therapy in Fabry disease: impact on clinical outcome?

1 reference

12 December 2020

High antibody titer in an adult with Pompe disease affects treatment with alglucosidase alfa

1 reference

12 December 2020

10.1097/GIM.0B013E3182174703

Identifiers

DOI

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Dimensions Publication ID

3 August 2017

1013219443

0 references

Fatcat ID

release_w3seibbcmrhtxc3zolrpr33mh4

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/w3seibbcmrhtxc3zolrpr33mh4

24 November 2022

mapped directly with Wikidata item

PMC publication ID

3954622

1 reference

3 August 2017

1 reference