(Q36105888)

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11 January 2020

review article

1 reference

title

In utero gene therapy: current challenges and perspectives (English)

1 reference

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11 January 2020

0 references

1

1 reference

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11 January 2020

Suzanne M Buckley

4

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11 January 2020

Jesús Prieto

7

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11 January 2020

author name string

M Gabriela Kramer

2

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11 January 2020

Ruben Hernandez-Alcoceba

3

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11 January 2020

Michael Themis

5

1 reference

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11 January 2020

Charles Coutelle

6

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11 January 2020

publication date

1 May 2005

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11 January 2020

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11 January 2020

volume

11

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11 January 2020

issue

5

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11 January 2020

page(s)

661-676

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The challenge of fetal gene therapy

11 January 2020

cites work

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Immune responses to gene therapy vectors: influence on vector function and effector mechanisms

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: tolerization of factor IX and vector antigens allows for long-term expression

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In-vivo retroviral gene transfer to the liver is cancelled by an immune response against the corrected cells. Can it be avoided?

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Neonatal or hepatocyte growth factor-potentiated adult gene therapy with a retroviral vector results in therapeutic levels of canine factor IX for hemophilia B.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Factors influencing in vivo transduction by recombinant adeno-associated viral vectors expressing the human factor IX cDNA.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Immune response to full-length dystrophin delivered to Dmd muscle by a high-capacity adenoviral vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Successful transgene expression with serial doses of aerosolized rAAV2 vectors in rhesus macaques

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Influence of vector dose on factor IX-specific T and B cell responses in muscle-directed gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Normal development of human fetal hematopoiesis between eight and seventeen weeks' gestation

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy progress and prospects: gene therapy of lysosomal storage disorders

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Reexpression following readministration of an adenoviral vector in adult mice after initial in utero adenoviral administration

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Induction of stable prenatal tolerance to beta-galactosidase by in utero gene transfer into preimmune sheep fetuses

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Permanent phenotypic correction of hemophilia B in immunocompetent mice by prenatal gene therapy.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Humoral immune response to recombinant adenovirus and adeno-associated virus after in utero administration of viral vectors in mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Neonatal gene transfer with a retroviral vector results in tolerance to human factor IX in mice and dogs

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

The burden of genetic disease on inpatient care in a children's hospital

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Urea-cycle disorders as a paradigm for inborn errors of hepatocyte metabolism

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

An autopsy case of ornithine transcarbamylase deficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

The effects of postponing prophylactic treatment on long-term outcome in patients with severe hemophilia

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Intravenous administration of an AAV-2 vector for the expression of factor IX in mice and a dog model of hemophilia B.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Efficient transduction of liver and muscle after in utero injection of lentiviral vectors with different pseudotypes

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long-term transgene expression by administration of a lentivirus-based vector to the fetal circulation of immuno-competent mice.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

A gene-deleted adenoviral vector results in phenotypic correction of canine hemophilia B without liver toxicity or thrombocytopenia

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Improved hepatic gene transfer by using an adeno-associated virus serotype 5 vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Organ weight in 684 adult autopsies: new tables for a Caucasoid population

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenovirus-mediated gene therapy for mucopolysaccharidosis VII: involvement of cross-correction in wide-spread distribution of the gene products and long-term effects of CTLA-4Ig coexpression

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prevalence of lysosomal storage disorders

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Mucopolysaccharidosis type VII in the developing mouse fetus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero injection of alpha-L-iduronidase-carrying retrovirus in canine mucopolysaccharidosis type I: infection of multiple tissues and neonatal gene expression

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Neuronal death is enhanced and begins during foetal development in type I spinal muscular atrophy spinal cord

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Rescue of neurodegeneration in Niemann-Pick C mice by a prion-promoter-driven Npc1 cDNA transgene

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenoviral expression of protein-L-isoaspartyl methyltransferase (PIMT) partially attenuates the biochemical changes in PIMT-deficient mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long-term correction of bilirubin UDPglucuronyltransferase deficiency in rats by in utero lentiviral gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Screening newborns for inborn errors of metabolism by tandem mass spectrometry

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prolonged metabolic correction in adult ornithine transcarbamylase-deficient mice with adenoviral vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

A pilot study of in vivo liver-directed gene transfer with an adenoviral vector in partial ornithine transcarbamylase deficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Onco-retroviral and lentiviral vector-based gene therapy for hemophilia: preclinical studies

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Inhibitor antibodies to factor VIII and factor IX: management

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

7 January 2021

Haemophilias A and B.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Myocardial fibrosis in mice with overexpression of human blood coagulation factor IX.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Short-term correction of factor VIII deficiency in a murine model of hemophilia A after delivery of adenovirus murine factor VIII in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy of muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Developmental progress in Duchenne muscular dystrophy: lessons for earlier detection.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Transduction of satellite cells after prenatal intramuscular administration of lentiviral vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Comparison of high-capacity and first-generation adenoviral vector gene delivery to murine muscle in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Newborn screening for cystic fibrosis: ensuring more good than harm

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Barriers to and new approaches for gene therapy and gene delivery in cystic fibrosis.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Foetal gene delivery in mice by intra-amniotic administration of retroviral producer cells and adenovirus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero recombinant adeno-associated virus gene transfer in mice, rats, and primates

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero gene transfer into the pulmonary epithelium

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene transfer into the fetal primate: evidence for the secretion of transgene product

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenoviral-mediated gene transfer to fetal pulmonary epithelia in vitro and in vivo.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Widespread and efficient marker gene expression in the airway epithelia of fetal sheep after minimally invasive tracheal application of recombinant adenovirus in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Lentiviral vector gene transfer into fetal rhesus monkeys (Macaca mulatta): lung-targeting approaches

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Reversal of cystic fibrosis phenotype in mice by gene therapy in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy for cystic fibrosis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy for cystic fibrosis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy progress and prospects: gene therapy for severe combined immunodeficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prenatal T-cell reconstitution after in utero transplantation with fetal liver cells in a patient with X-linked severe combined immunodeficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Retinal degeneration in Aipl1-deficient mice: a new genetic model of Leber congenital amaurosis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero gene therapy rescues vision in a murine model of congenital blindness

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Novel and recurrent mutations in the laminin-5 genes causing lethal junctional epidermolysis bullosa: molecular basis and clinical course of Herlitz disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Fetal wound healing: current biology

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Major hematologic diseases in the developing world- new aspects of diagnosis and management of thalassemia, malarial anemia, and acute leukemia.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero gene therapy: transfer and long-term expression of the bacterial neo(r) gene in sheep after direct injection of retroviral vectors into preimmune fetuses

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Successful expression of beta-galactosidase and factor IX transgenes in fetal and neonatal sheep after ultrasound-guided percutaneous adenovirus vector administration into the umbilical vein

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Reduced toxicity of F-deficient Sendai virus vector in the mouse fetus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Comparison of gene expression after intraperitoneal delivery of AAV2 or AAV5 in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long‐term transgene expression in cardiac and skeletal muscle following fetal administration of adenoviral or adeno‐associated viral vectors in mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenovirus-mediated prenatal gene transfer to murine central nervous system

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

High-efficiency, long-term cardiac expression of foreign genes in living mouse embryos and neonates.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenovirus-mediated gene transfer to the peritoneum and hepatic parenchyma of fetal mice in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenovirus-mediated gene transfer in the midgestation fetal mouse

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long-term gene transfer to mouse fetuses with recombinant adenovirus and adeno-associated virus (AAV) vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Ultrasound-guided percutaneous delivery of adenoviral vectors encoding the beta-galactosidase and human factor IX genes to early gestation fetal sheep in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In utero transfer and expression of exogenous genes in sheep

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Rhesus monkey model for fetal gene transfer: studies with retroviral- based vector systems

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

A preliminary evaluation of recombinant adeno-associated virus biodistribution in rhesus monkeys after intrahepatic inoculation in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene transfection into fetal sheep airways in utero using guanidinium-cholesterol cationic lipids

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Intraamniotic administration of an adenoviral vector for gene transfer to fetal sheep and mouse tissues

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Widespread gene transduction to the central nervous system by adenovirus in utero: implication for prenatal gene therapy to brain involvement of lysosomal storage disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Intrahepatic vein fetal blood sampling: current role in prenatal diagnosis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

BAPS Prize--1997. Fetal gene therapy: efficacy, toxicity, and immunologic effects of early gestation recombinant adenovirus. British Association of Paediatric Surgeons

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Intrauterine gene transfer: gestational stage-specific gene delivery in mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Persistent postnatal transgene expression in both muscle and liver after fetal injection of recombinant adenovirus.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Comparative placental structure

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Temporally regulated expression patterns following in utero adenovirus-mediated gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Adenovirus-mediated in utero gene transfer in mice and guinea pigs: tissue distribution of recombinant adenovirus determined by quantitative TaqMan-polymerase chain reaction assay

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Ultrasound-guided gene transfer to hepatocytes in utero.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Fetomaternal cell traffic, pregnancy-associated progenitor cells, and autoimmune disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Materno-foetal transfer of H. influenzae and pneumococcal antibodies is influenced by prematurity and low birth weight: implications for conjugate vaccine trials

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Natural materno-fetal transfer of antibodies to PspA and to PsaA.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prenatal transfer of low amounts of herpes simplex virus (HSV)-specific antibody protects newborn mice against HSV infection during acute maternal stress

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Dynamics of immunoglobulins at the feto-maternal interface

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Effect of adeno-associated virus-specific immunoglobulin G in human amniotic fluid on gene transfer.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Comparative developmental anatomy of the murine and human definitive placentae.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Species comparison of anatomical and functional immune system development

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Fetoscopic tracheal occlusion (FETO) for severe congenital diaphragmatic hernia: evolution of a technique and preliminary results.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Intrauterine transfusion--intraperitoneal versus intravascular approach: a case-control comparison

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Perinatal fetal-cell and gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Sustained human factor VIII expression in hemophilia A mice following systemic delivery of a gutless adenoviral vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Transposition from a gutless adeno-transposon vector stabilizes transgene expression in vivo

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Integration efficiency of a hybrid adenoretroviral vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long-term transgene expression in proliferating cells mediated by episomally maintained high-capacity adenovirus vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Sustained delivery of therapeutic concentrations of human clotting factor IX--a comparison of adenoviral and AAV vectors administered in utero

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Long term physiologic modification using rAAV in utero gene-therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

AAV serotype 2 vectors preferentially integrate into active genes in mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Evidence for infection of the human embryo with adeno-associated virus in pregnancy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Introduction of a selectable gene into different animal tissue by a retrovirus recombinant vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

The ras and myc oncogenes cooperate in tumor induction in many tissues when introduced into midgestation mouse embryos by retroviral vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Maternal transmission of retroviral disease: transgenic mice as a rapid test system for evaluating perinatal and transplacental antiretroviral therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Widespread Dispersion of Neuronal Clones Across Functional Regions of the Cerebral Cortex

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Efficient lentiviral transduction of liver requires cell cycling in vivo

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Nonviral gene transfer into fetal mouse livers (a comparison between the cationic polymer PEI and naked DNA).

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In Utero Hematopoietic Stem Cell Transplantation in Nonhuman Primates: The Role of T Cells

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy for canine alpha-L-iduronidase deficiency: in utero adoptive transfer of genetically corrected hematopoietic progenitors results in engraftment but not amelioration of disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Amphotropic and ecotropic retroviral vector viruses transduce midgestational murine fetal liver cells in a dual-chambered cocultivation system

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prenatal gene tranfer: scientific, medical, and ethical issues: a report of the Recombinant DNA Advisory Committee

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Human fetal gene therapy: moral and ethical questions

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

On the scientific and ethical issues of fetal somatic gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Insertional oncogenesis in gene therapy: how much of a risk?

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Retroviral vector integration occurs in preferred genomic targets of human bone marrow-repopulating cells

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Conditional site-specific integration into human chromosome 19 by using a ligand-dependent chimeric adeno-associated virus/Rep protein

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Phage integrases for the construction and manipulation of transgenic mammals

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Epstein-Barr virus vectors provide prolonged robust factor IX expression in mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

In vitro and in vivo delivery of intact BAC DNA -- comparison of different methods

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Systemic diffusion including germ cells after plasmidic in utero gene transfer in the rat.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Development, morphology, and function of the yolk-sac placenta of laboratory rodents

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Prp-c and Prp-Sc at the fetal-maternal interface

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Anatomy, physiology and pathology of the amniotic and allantoic compartments in the sheep and cow.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gender, death and cystic fibrosis: is energy expenditure a component?

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Survival in Duchenne muscular dystrophy: improvements in life expectancy since 1967 and the impact of home nocturnal ventilation

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Burden of genetic disorders in India

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Survival of children with sickle cell disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Complications of beta-thalassemia major in North America

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Survival in medically treated patients with homozygous beta-thalassemia

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Gene therapy for severe combined immune deficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Alpha-1 antitrypsin deficiency is not a rare disease but a disease that is rarely diagnosed

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

A Phase 1 Trial of Riluzole in Spinal Muscular Atrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Diagnosis and management of Crigler-Najjar syndrome

7 January 2021

2 references

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

7 January 2021

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

inferred from DOI database lookup

7 January 2021

based on heuristic

Ornithine carbamoyltransferase deficiency

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Incidence of inborn errors of metabolism in British Columbia, 1969-1996.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Management of phenylketonuria for optimal outcome: a review of guidelines for phenylketonuria management and a report of surveys of parents, patients, and clinic directors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Severe type II Gaucher disease with ichthyosis, arthrogryposis and neuronal apoptosis: molecular and pathological analyses

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Enzyme replacement in Gaucher disease

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Outcome of second hematopoietic cell transplantation in Hurler syndrome.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Molecular pathophysiology in Tay-Sachs and Sandhoff diseases as revealed by gene expression profiling

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Molecular genetics of Leber congenital amaurosis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Junctional epidermolysis bullosa gravis (Herlitz): diagnostic and genetic aspects

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

The clinical spectrum of dystrophic epidermolysis bullosa

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

The clinical spectrum of epidermolysis bullosa simplex

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

Passage through mitosis is required for oncoretroviruses but not for the human immunodeficiency virus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2005.01.015

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1016/J.YMTHE.2005.01.015

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15851005%20AND%20SRC:MED&resulttype=core&format=json

11 January 2020

1 reference