(Q36754605)
Statements
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Impaired clearance of accumulated lysosomal glycogen in advanced Pompe disease despite high-level vector-mediated transgene expression (English)
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Baodong Sun
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Haoyue Zhang
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Andrew Bird
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Songtao Li
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Sarah P Young
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Dwight D Koeberl
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1 October 2009
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913-920
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Identifiers
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