(Q45876651)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:22278413%20AND%20SRC:MED&resulttype=core&format=json

21 January 2020

title

Systemic delivery of scAAV9 in fetal macaques facilitates neuronal transduction of the central and peripheral nervous systems (English)

1 reference

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21 January 2020

2

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21 January 2020

Arijit Biswas

3

1 reference

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21 January 2020

Suzanne M Buckley

10

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21 January 2020

author name string

C N Mattar

1

1 reference

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21 January 2020

N Johana

4

1 reference

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21 January 2020

X W Ng

5

1 reference

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21 January 2020

A S Fisk

6

1 reference

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21 January 2020

L G Tan

8

1 reference

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21 January 2020

A A Rahim

9

1 reference

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21 January 2020

M H Tan

11

1 reference

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21 January 2020

J Lu

12

1 reference

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21 January 2020

M Choolani

13

1 reference

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21 January 2020

J K Y Chan

14

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21 January 2020

N M Fisk

7

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21 January 2020

language of work or name

1 reference

26 January 2012

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21 January 2020

1 reference

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21 January 2020

volume

20

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21 January 2020

issue

1

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21 January 2020

page(s)

69-83

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https://scigraph.springernature.com/pub.10.1038/gt.2011.216

21 January 2020

exact match

0 references

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Reversal of motor impairments in parkinsonian rats by continuous intrastriatal delivery of L-dopa using rAAV-mediated gene transfer

21 January 2018

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Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral-mediated gene transfer.

21 January 2018

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CNS-directed AAV2-mediated gene therapy ameliorates functional deficits in a murine model of infantile neuronal ceroid lipofuscinosis.

21 January 2018

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Adeno-associated virus vector genomes persist as episomal chromatin in primate muscle

21 January 2018

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Widespread correction of lysosomal storage in the mucopolysaccharidosis type VII mouse brain with a herpes simplex virus type 1 vector expressing beta-glucuronidase

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Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8.

21 January 2018

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Clades of Adeno-associated viruses are widely disseminated in human tissues.

21 January 2018

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Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

21 January 2018

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Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to differential targeting of CNS cell types and extensive transduction of the nervous system.

21 January 2018

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RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

21 January 2018

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Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons

21 January 2018

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Failure of SCID-X1 gene therapy in older patients

21 January 2018

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Tight junctions of the blood-brain barrier: development, composition and regulation

21 January 2018

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Gene therapy progress and prospects: fetal gene therapy--first proofs of concept--some adverse effects

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In utero gene therapy: current challenges and perspectives.

21 January 2018

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Genetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VII.

21 January 2018

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Of mice and not men: differences between mouse and human immunology

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Correction of neurological disease of mucopolysaccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery

21 January 2018

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Comparison of adeno-associated viral vector serotypes for spinal cord and motor neuron gene delivery

21 January 2018

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Systemic gene delivery in large species for targeting spinal cord, brain, and peripheral tissues for pediatric disorders

21 January 2018

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microRNA122-regulated transgene expression increases specificity of cardiac gene transfer upon intravenous delivery of AAV9 vectors

21 January 2018

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Engineering liver-detargeted AAV9 vectors for cardiac and musculoskeletal gene transfer

21 January 2018

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21 January 2018

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Preclinical differences of intravascular AAV9 delivery to neurons and glia: a comparative study of adult mice and nonhuman primates

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Optimizing promoters for recombinant adeno-associated virus-mediated gene expression in the peripheral and central nervous system using self-complementary vectors

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Successful expression of beta-galactosidase and factor IX transgenes in fetal and neonatal sheep after ultrasound-guided percutaneous adenovirus vector administration into the umbilical vein

21 January 2018

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In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor

21 January 2018

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Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B mice

21 January 2018

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MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression

21 January 2018

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The eye and inherited metabolic disease: a review.

21 January 2018

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Comprehensive analysis of photoreceptor gene expression and the identification of candidate retinal disease genes

21 January 2018

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Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration

21 January 2018

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21 January 2018

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Abetalipoproteinemia: two case reports and literature review

21 January 2018

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Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

21 January 2018

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Improved metabolic correction in patients with lysosomal storage disease treated with hematopoietic stem cell transplant compared with enzyme replacement therapy

21 January 2018

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7 January 2021

Hematopoietic stem-cell transplantation in globoid-cell leukodystrophy

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https://api.crossref.org/works/10.1038%2FGT.2011.216

7 January 2021

Peroxisomal disorders: genotype, phenotype, major neuropathologic lesions, and pathogenesis.

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7 January 2021

A classification of pregnancy losses after invasive prenatal diagnostic procedures: an approach to allow comparison of units with a different case mix

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https://api.crossref.org/works/10.1038%2FGT.2011.216

7 January 2021

Fetoscopy guided by real-time ultrasound for pure fetal blood samples, fetal skin samples, and examination of the fetus in utero

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https://api.crossref.org/works/10.1038%2FGT.2011.216

7 January 2021

AAV8-mediated hepatic gene transfer in infant rhesus monkeys (Macaca mulatta)

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https://api.crossref.org/works/10.1038%2FGT.2011.216

7 January 2021

Induction of stable prenatal tolerance to beta-galactosidase by in utero gene transfer into preimmune sheep fetuses

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7 January 2021

Sustained AAV-mediated dystrophin expression in a canine model of Duchenne muscular dystrophy with a brief course of immunosuppression

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7 January 2021