(Q45881645)
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Antisense RNA sequences modulating the ataxin-1 message: molecular model of gene therapy for spinocerebellar ataxia type 1, a dominant-acting unstable trinucleotide repeat disease (English)
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Youxin Gao
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Tao Zu
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Walter C Low
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Harry T Orr
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R Scott McIvor
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1 January 2008
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