(Q45886876)

17 December 2017

title

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX. (English)

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17 December 2017

main subject

hemophilia

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coagulation factor IX

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4

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17 December 2017

author name string

Bigger BW

1

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17 December 2017

Siapati EK

2

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17 December 2017

Mistry A

3

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17 December 2017

Nivsarkar MS

5

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17 December 2017

Jacobs L

6

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17 December 2017

Perrett R

7

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17 December 2017

Holder MV

8

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17 December 2017

Ridler C

9

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17 December 2017

Kemball-Cook G

10

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17 December 2017

Ali RR

11

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17 December 2017

Forbes SJ

12

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17 December 2017

Coutelle C

13

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17 December 2017

Wright N

14

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17 December 2017

Alison M

15

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17 December 2017

Thrasher AJ

16

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17 December 2017

Bonnet D

17

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17 December 2017

Themis M

18

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17 December 2017

publication date

1 January 2006

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17 December 2017

published in

Gene Therapy

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17 December 2017

volume

13

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17 December 2017

page(s)

117-126

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17 December 2017

issue

2

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17 December 2017

https://scigraph.springernature.com/pub.10.1038/sj.gt.3302638

exact match

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cites work

Haemophilia B mutations in Sweden: a population-based study of mutational heterogeneity

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Development of inhibitors in patients with haemophilia from India

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Factor IX inhibitors and anaphylaxis in hemophilia B.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Anaphylactoid reactions and nephrotic syndrome--a considerable risk during factor IX treatment in patients with haemophilia B and inhibitors: a report on the outcome in two brothers

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Efficient production of human FVIII in hemophilic mice using lentiviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Sustained phenotypic correction of hemophilia a mice following oncoretroviral-mediated expression of a bioengineered human factor VIII gene in long-term hematopoietic repopulating cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

T cells mediate resistance to genetically modified bone marrow in lethally irradiated recipients

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Induction of T-cell tolerance to an MHC class I alloantigen by gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Induction of T cell tolerance to a protein expressed in the cytoplasm through retroviral‐mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

High-level transduction and gene expression in hematopoietic repopulating cells using a human immunodeficiency [correction of imunodeficiency] virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Distinct classes of human stem cells that differ in proliferative and self-renewal potential

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Permanent phenotypic correction of hemophilia B in immunocompetent mice by prenatal gene therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Comparison of HIV- and EIAV-based vectors on their efficiency in transducing murine and human hematopoietic repopulating cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Optimal protocol for total body irradiation for allogeneic bone marrow transplantation in mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Myeloablation enhances engraftment of transduced murine hematopoietic cells, but does not influence long-term expression of the transgene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Aberrant DAP12 signaling in the 129 strain of mice: implications for the analysis of gene-targeted mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Retroviral Transfer of Donor MHC Class I or MHC Class II Genes into Recipient Bone Marrow Cells Can Induce Operational Tolerance to AlloantigensIn Vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Adenoviral transfer of a single donor-specific MHC class I gene to recipient bone marrow cells can induce specific immunological unresponsiveness in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Use of gene therapy to suppress the antigen-specific immune responses in mice to an HLA antigen

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Transplantation tolerance by donor MHC gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Engraftment of retroviral EGFP-transduced bone marrow in mice prevents rejection of EGFP-transgenic skin grafts.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Mechanisms of transplant tolerance induction using costimulatory blockade

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Induction of antigen-specific tolerance to bone marrow allografts with CD4+CD25+ T lymphocytes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Myeloablation is not required to select and maintain expression of the drug-resistance gene, mutant MGMT, in primary and secondary recipients

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Production of human clotting Factor IX without toxicity in mice after vascular delivery of a lentiviral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

A factor IX-deficient mouse model for hemophilia B gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Blocking both signal 1 and signal 2 of T-cell activation prevents apoptosis of alloreactive T cells and induction of peripheral allograft tolerance

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

Induction of stable long-term mixed hematopoietic chimerism following nonmyeloablative conditioning with T cell-depleting antibodies, cyclophosphamide, and thymic irradiation leads to donor-specific in vitro and in vivo tolerance

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

inferred from DOI database lookup

7 January 2021

based on heuristic

Engraftment assessment in human and mouse liver tissue after sex-mismatched liver cell transplantation by real-time quantitative PCR for Y chromosome sequences

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302638

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/SJ.GT.3302638

1 reference

17 December 2017

Dimensions Publication ID

0 references

1 reference

17 December 2017