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Gene therapy through autologous transplantation of gene-modified hematopoietic stem cells
scientific article
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instance of
scholarly article
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
title
Gene therapy through autologous transplantation of gene-modified hematopoietic stem cells
(English)
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
main subject
gene therapy
0 references
author
Donald B. Kohn
series ordinal
1
1 reference
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
author name string
Sung-Yun Pai
series ordinal
2
2 references
stated in
Crossref
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
Michel Sadelain
series ordinal
3
2 references
stated in
Crossref
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
language of work or name
English
1 reference
stated in
PubMed
publication date
29 September 2012
1 reference
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
published in
Biology of Blood and Marrow Transplantation
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
volume
19
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
issue
1 Suppl
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
page(s)
S64-9
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
cites work
Concise review: managing genotoxicity in the therapeutic modification of stem cells
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Transplantation of hematopoietic stem cells in human severe combined immunodeficiency: longterm outcomes
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
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Thymic lymphoproliferative disease after successful correction of CD40 ligand deficiency by gene transfer in mice
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
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inferred from DOI database lookup
Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
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inferred from DOI database lookup
Mechanism of reduction in titers from lentivirus vectors carrying large inserts in the 3'LTR.
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
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inferred from DOI database lookup
Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Genome-wide high-throughput integrome analyses by nrLAM-PCR and next-generation sequencing
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Stem-cell transplantation for sickle cell disease
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Gene therapy for immunodeficiency due to adenosine deaminase deficiency.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Allogeneic hematopoietic stem-cell transplantation for sickle cell disease
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Efficacy of gene therapy for X-linked severe combined immunodeficiency
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Stem-cell gene therapy for the Wiskott-Aldrich syndrome
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
High-level beta-globin expression after retroviral transfer of locus activation region-containing human beta-globin gene derivatives into murine erythroleukemia cells
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
A method to sequence and quantify DNA integration for monitoring outcome in gene therapy
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Genetic strategies for the treatment of sickle cell anaemia
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Strategy for a multicenter phase I clinical trial to evaluate globin gene transfer in beta-thalassemia
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Transcription start regions in the human genome are favored targets for MLV integration
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Gene therapy in peripheral blood lymphocytes and bone marrow for ADA- immunodeficient patients
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Correction of a mouse model of sickle cell disease: lentiviral/antisickling beta-globin gene transduction of unmobilized, purified hematopoietic stem cells
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
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7 January 2021
based on heuristic
inferred from DOI database lookup
Therapeutic levels of fetal hemoglobin in erythroid progeny of β-thalassemic CD34+ cells after lentiviral vector-mediated gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Transplantation in patients with SCID: mismatched related stem cells or unrelated cord blood?
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FJ.BBMT.2012.09.021
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Identifiers
DOI
10.1016/J.BBMT.2012.09.021
1 reference
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
PubMed publication ID
23032601
2 references
stated in
PubMed
stated in
Europe PubMed Central
PubMed publication ID
23032601
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23032601%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 March 2020
ResearchGate publication ID
231862681
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