(Q33770970)

English

Absence of a desmopressin response after therapeutic expression of factor VIII in hemophilia A dogs with liver-directed neonatal gene therapy

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scholarly article

1 reference

Europe PubMed Central

29 July 2017

Absence of a desmopressin response after therapeutic expression of factor VIII in hemophilia A dogs with liver-directed neonatal gene therapy (English)

1 reference

Europe PubMed Central

29 July 2017

0 references

0 references

Coagulation factor VIII

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0 references

1 reference

based on heuristic

inferred from title

author name string

Lingfei Xu

1

1 reference

Europe PubMed Central

29 July 2017

Timothy C Nichols

2

1 reference

Europe PubMed Central

29 July 2017

Rita Sarkar

3

1 reference

Europe PubMed Central

29 July 2017

Stephanie McCorquodale

4

1 reference

Europe PubMed Central

29 July 2017

Dwight A Bellinger

5

1 reference

Europe PubMed Central

29 July 2017

Katherine P Ponder

6

1 reference

Europe PubMed Central

29 July 2017

language of work or name

0 references

publication date

18 April 2005

1 reference

Europe PubMed Central

29 July 2017

Proceedings of the National Academy of Sciences of the United States of America

1 reference

Europe PubMed Central

29 July 2017

102

1 reference

Europe PubMed Central

29 July 2017

17

1 reference

Europe PubMed Central

29 July 2017

6080-6085

1 reference

Europe PubMed Central

29 July 2017

Sustained phenotypic correction of hemophilia a mice following oncoretroviral-mediated expression of a bioengineered human factor VIII gene in long-term hematopoietic repopulating cells

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Gene therapy of the hemophilias

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Prospects for gene therapy of haemophilia

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Clinical gene transfer studies for hemophilia A.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Helper-dependent adenoviral vectors mediate therapeutic factor VIII expression for several months with minimal accompanying toxicity in a canine model of severe hemophilia A

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Cellular mechanisms of the hemostatic effects of desmopressin (DDAVP).

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Comparative response of plasma VWF in dogs to up-regulation of VWF mRNA by interleukin-11 versus Weibel-Palade body release by desmopressin (DDAVP).

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Desmopressin in mild hemophilia A: indications, limitations, efficacy, and safety

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

The Chapel Hill hemophilia A dog colony exhibits a factor VIII gene inversion

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Hemophilia gene therapy: update

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Evaluation of the duration of human factor VIII expression in nonhuman primates after systemic delivery of an adenoviral vector

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Genetic induction of a releasable pool of factor VIII in human endothelial cells

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Further characterization of factor VIII-deficient mice created by gene targeting: RNA and protein studies

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Quantitative analysis of von Willebrand factor propeptide release in vivo: effect of experimental endotoxemia and administration of 1-deamino-8-D-arginine vasopressin in humans

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

The development of homologous (canine/anti-canine) antibodies in dogs with haemophilia A (factor VIII deficiency): a ten-year longitudinal study.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Liver transplantation in hemophilia A

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

4 July 2018

Sustained human factor VIII expression in hemophilia A mice following systemic delivery of a gutless adenoviral vector

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Factors influencing therapeutic efficacy and the host immune response to helper-dependent adenoviral gene therapy in hemophilia A mice

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Adenovirus-mediated factor VIII gene expression results in attenuated anti-factor VIII-specific immunity in hemophilia A mice compared with factor VIII protein infusion

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Naked DNA transfer of Factor VIII induced transgene-specific, species-independent immune response in hemophilia A mice

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Expression of human factor VIII by splicing between dimerized AAV vectors

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Dual vectors expressing murine factor VIII result in sustained correction of hemophilia A mice

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Phenotype correction of hemophilia A mice by spliceosome-mediated RNA trans-splicing

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Phenotypic correction of a mouse model of hemophilia A using AAV2 vectors encoding the heavy and light chains of FVIII.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Use of blood outgrowth endothelial cells for gene therapy for hemophilia A.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Sustained phenotypic correction of canine hemophilia A using an adeno-associated viral vector

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Systemic delivery of an adenoviral vector encoding canine factor VIII results in short-term phenotypic correction, inhibitor development, and biphasic liver toxicity in hemophilia A dogs.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Is the incidence and prevalence of inhibitors greater with recombinant products? No.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Neonatal or hepatocyte growth factor-potentiated adult gene therapy with a retroviral vector results in therapeutic levels of canine factor IX for hemophilia B.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Neonatal gene transfer with a retroviral vector results in tolerance to human factor IX in mice and dogs

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Transduction of hepatocytes after neonatal delivery of a Moloney murine leukemia virus based retroviral vector results in long-term expression of beta-glucuronidase in mucopolysaccharidosis VII dogs

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Partial correction of murine hemophilia A with neo-antigenic murine factor VIII.

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

In vivo recovery with products of very high purity--assay discrepancies

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Expression of factor VIII by murine liver sinusoidal endothelial cells

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0409249102

21 January 2018

Therapeutic levels of human factor VIII and IX using HIV-1-based lentiviral vectors in mouse liver

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

30 October 2018

Sustained high-level expression of full-length human factor VIII and restoration of clotting activity in hemophilic mice using a minimal adenovirus vector.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1087916

30 October 2018

Gene transfer as an approach to treating hemophilia

1 reference

https://pubmed.ncbi.nlm.nih.gov/15837921

12 December 2020

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Identifiers

10.1073/PNAS.0409249102

1 reference

Europe PubMed Central

29 July 2017

2005PNAS..102.6080X

0 references

1 reference

Europe PubMed Central

29 July 2017

1 reference

Europe PubMed Central

29 July 2017

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