(Q35533589)

8 August 2017

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells (English)

1 reference

8 August 2017

0 references

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Aaron Cooper

11

1 reference

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4 June 2020

Andrew Wilber

19

1 reference

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4 June 2020

Donald B. Kohn

25

1 reference

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4 June 2020

Megan D Hoban

1

1 reference

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4 June 2020

Zulema Romero

4

1 reference

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4 June 2020

Michael L Kaufman

5

1 reference

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4 June 2020

Michelle Ho

7

1 reference

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4 June 2020

David Gray

9

1 reference

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4 June 2020

Georgia R Lill

10

1 reference

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4 June 2020

Philip D Gregory

21

1 reference

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4 June 2020

18

Edward J Rebar

1 reference

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4 June 2020

16

David E Paschon

1 reference

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4 June 2020

23

Andreas Reik

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

15

Pei-Qi Liu

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

17

Lei Zhang

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

author name string

Matthew C Mendel

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

Alok V Joglekar

6

1 reference

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4 June 2020

Dianne Lumaquin

8

1 reference

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4 June 2020

Fabrizia Urbinati

12

1 reference

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4 June 2020

Shantha Senadheera

13

1 reference

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4 June 2020

Allen Zhu

14

1 reference

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4 June 2020

Xiaoyan Wang

20

1 reference

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4 June 2020

Michael C Holmes

22

1 reference

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4 June 2020

Roger P Hollis

24

1 reference

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4 June 2020

language of work or name

English

0 references

publication date

2 March 2015

1 reference

8 August 2017

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

volume

125

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

issue

17

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

page(s)

2597-2604

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

Targeted genome editing in human repopulating haematopoietic stem cells

4 June 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Gene editing of CCR5 in autologous CD4 T cells of persons infected with HIV

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Gene therapy for hemoglobinopathies: the state of the field and the future

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Safe mobilization of CD34+ cells in adults with β-thalassemia and validation of effective globin gene transfer for clinical investigation.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Nuclease-mediated gene editing by homologous recombination of the human globin locus

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

β-globin gene transfer to human bone marrow for sickle cell disease.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Integrase-defective lentiviral vectors as a delivery platform for targeted modification of adenosine deaminase locus

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

The natural history of sickle cell disease

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Mechanisms of retroviral integration and mutagenesis

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

In situ genetic correction of the sickle cell anemia mutation in human induced pluripotent stem cells using engineered zinc finger nucleases

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Proof of principle for transfusion of in vitro-generated red blood cells.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Site-specific gene correction of a point mutation in human iPS cells derived from an adult patient with sickle cell disease

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

An unbiased genome-wide analysis of zinc-finger nuclease specificity

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

High-frequency genome editing using ssDNA oligonucleotides with zinc-finger nucleases

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

In mixed hematopoietic chimerism, the donor red cells win.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Hematopoietic stem cell quiescence promotes error-prone DNA repair and mutagenesis

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Global epidemiology of haemoglobin disorders and derived service indicators

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Creation of "humanized" mice to study human immunity

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Transient gene expression by nonintegrating lentiviral vectors

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Outcome of sickle cell anemia: a 4-decade observational study of 1056 patients

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Highly efficient endogenous human gene correction using designed zinc-finger nucleases

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Ex vivo generation of fully mature human red blood cells from hematopoietic stem cells

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Chromosomal site-specific double-strand breaks are efficiently targeted for repair by oligonucleotides in yeast

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Introduction of double-strand breaks into the genome of mouse cells by expression of a rare-cutting endonuclease

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Seamless correction of the sickle cell disease mutation of the HBB gene in human induced pluripotent stem cells using TALENs

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Outcomes, utilization, and costs among thalassemia and sickle cell disease patients receiving deferoxamine therapy in the United States.

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Small fragment homologous replacement-mediated modification of genomic beta-globin sequences in human hematopoietic stem/progenitor cells

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

Stable mixed hematopoietic chimerism after bone marrow transplantation for sickle cell anemia.

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4408287

10.1182/BLOOD-2014-12-615948

26 September 2018

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25733580%20AND%20SRC:MED&resulttype=core&format=json

4 June 2020

1 reference