(Q36143241)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

title

In vivo genome editing of the albumin locus as a platform for protein replacement therapy (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Xavier M Anguela

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Yannick Doyon

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Philip D Gregory

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Katherine A. High

16

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

15

Edward J Rebar

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

7

David E Paschon

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

10

David Shivak

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

author name string

Thomas Wechsler

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Russell C DeKelver

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Scott Sproul

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Jeffrey C Miller

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Robert J Davidson

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Shangzhen Zhou

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Julianne Rieders

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Michael C Holmes

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

language of work or name

English

0 references

publication date

21 August 2015

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

volume

126

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

issue

15

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

page(s)

1777-1784

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

Long-term safety and efficacy of factor IX gene therapy in hemophilia B.

22 February 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Promoterless gene targeting without nucleases ameliorates haemophilia B in mice.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Gene editing of CCR5 in autologous CD4 T cells of persons infected with HIV

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Robust ZFN-mediated genome editing in adult hemophilic mice.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Minimal modification in the factor VIII B-domain sequence ameliorates the murine hemophilia A phenotype

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

AAV2 gene therapy readministration in three adults with congenital blindness.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Adenovirus-associated virus vector-mediated gene transfer in hemophilia B

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector.

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Revealing off-target cleavage specificities of zinc-finger nucleases by in vitro selection

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

In vivo genome editing restores haemostasis in a mouse model of haemophilia

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Vector characterization methods for quality control testing of recombinant adeno-associated viruses

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Enhancing zinc-finger-nuclease activity with improved obligate heterodimeric architectures

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Efficient gene targeting mediated by adeno-associated virus and DNA double-strand breaks

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Analysis of Relative Gene Expression Data Using Real-Time Quantitative PCR and the 2−ΔΔCT Method

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Targeted genome editing in human repopulating haematopoietic stem cells

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Overcoming preexisting humoral immunity to AAV using capsid decoys

2 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Introduction of double-strand breaks into the genome of mouse cells by expression of a rare-cutting endonuclease

2 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency

2 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Engineering a novel secretion signal for cross-host recombinant protein expression

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4600017

Hurler and Hunter syndromes: mutual correction of the defect in cultured fibroblasts

23 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26297739

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Novel forms of B-domain-deleted recombinant factor VIII molecules. Construction and biochemical characterization

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/26297739

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1182/BLOOD-2014-12-615492

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26297739%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

1 reference