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Recent gene therapy advancements for neurological diseases.
scientific article published on February 2013
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Europe PubMed Central
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5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
retrieved
24 February 2020
title
Recent gene therapy advancements for neurological diseases
(English)
1 reference
stated in
Europe PubMed Central
PMC publication ID
5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
main subject
gene therapy
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Sahana Nagabhushan Kalburgi
series ordinal
1
1 reference
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Europe PubMed Central
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5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
Nadia N Khan
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2
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Europe PubMed Central
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5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
Steven J Gray
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3
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5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
publication date
1 February 2013
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retrieved
24 February 2020
published in
Discovery Medicine
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Europe PubMed Central
PMC publication ID
5554939
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
volume
15
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Europe PubMed Central
PMC publication ID
5554939
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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
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24 February 2020
issue
81
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Europe PubMed Central
PMC publication ID
5554939
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24 February 2020
page(s)
111-119
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5554939
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retrieved
24 February 2020
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Persistence of high-capacity adenoviral vectors as replication-defective monomeric genomes in vitro and in murine liver
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Stable gene transfer to muscle using non-integrating lentiviral vectors
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Efficient transduction of neurons using Ross River glycoprotein-pseudotyped lentiviral vectors.
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PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
14 September 2017
Production and neurotropism of lentivirus vectors pseudotyped with lyssavirus envelope glycoproteins.
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
28 September 2017
Gene therapy for neurologic disease
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
28 September 2017
Correction of neurological disease of mucopolysaccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
23 June 2018
Gene therapy of x-linked adrenoleukodystrophy using hematopoietic stem cells and a lentiviral vector
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
23 June 2018
Quantitative analysis of the packaging capacity of recombinant adeno-associated virus
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
23 June 2018
Demonstration of circularization of herpes simplex virus DNA following infection using pulsed field gel electrophoresis
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
23 June 2018
Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Efficient gene delivery to the adult and fetal CNS using pseudotyped non-integrating lentiviral vectors.
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome.
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Immune responses to AAV in a phase I study for Canavan disease
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Transduction characteristics of adeno-associated virus vectors expressing cap serotypes 7, 8, 9, and Rh10 in the mouse brain
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Recombinant AAV viral vectors pseudotyped with viral capsids from serotypes 1, 2, and 5 display differential efficiency and cell tropism after delivery to different regions of the central nervous system
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Outcome of 27 patients with Hurler's syndrome transplanted from either related or unrelated haematopoietic stem cell sources
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Functional amelioration of murine galactosialidosis by genetically modified bone marrow hematopoietic progenitor cells
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Toxicity of a first-generation adenoviral vector in rhesus macaques
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Targeting gene-modified hematopoietic cells to the central nervous system: use of green fluorescent protein uncovers microglial engraftment.
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Acute direct adenoviral vector cytotoxicity and chronic, but not acute, inflammatory responses correlate with decreased vector-mediated transgene expression in the brain
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
Evaluation of genetically engineered herpes simplex viruses as oncolytic agents for human malignant brain tumors.
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5554939
retrieved
31 August 2018
[Gene therapy of adrenoleukodystrophy]
1 reference
stated in
PubMed
reference URL
https://pubmed.ncbi.nlm.nih.gov/23449113
retrieved
12 December 2020
based on heuristic
inferred from PubMed ID database lookup
The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update
1 reference
stated in
PubMed
reference URL
https://pubmed.ncbi.nlm.nih.gov/23449113
retrieved
12 December 2020
based on heuristic
inferred from PubMed ID database lookup
Gene therapy for lysosomal storage disorders
1 reference
stated in
PubMed
reference URL
https://pubmed.ncbi.nlm.nih.gov/23449113
retrieved
12 December 2020
based on heuristic
inferred from PubMed ID database lookup
Identifiers
PMC publication ID
5554939
1 reference
stated in
Europe PubMed Central
PMC publication ID
5554939
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
retrieved
24 February 2020
PubMed publication ID
23449113
1 reference
stated in
Europe PubMed Central
PMC publication ID
5554939
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23449113%20AND%20SRC:MED&resulttype=core&format=json
retrieved
24 February 2020
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