(Q40375767)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

title

CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

X-linked chronic granulomatous disease

9 April 2020

main subject

CRISPR

0 references

0 references

0 references

18

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Harry Malech

20

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

1

Suk See De Ravin

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

17

Douglas Kuhns

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

4

Uimook Choi

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

11

Colin Sweeney

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

6

Sherry Koontz

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

19

Madhusudan V Peshwa

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

12

Lela Kardava

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

author name string

Linhong Li

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Xiaolin Wu

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Cornell Allen

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Janet Lee

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Narda Theobald-Whiting

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Jessica Chu

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Mary Garofalo

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Angelia Viley

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Pachai Natarajan

15

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Ling Su

16

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

Susan Moir

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

language of work or name

English

0 references

publication date

1 January 2017

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

Science Translational Medicine

9 April 2020

published in

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

volume

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

issue

372

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

Comparison of outcomes of hematopoietic stem cell transplantation without chemotherapy conditioning by using matched sibling and unrelated donors for treatment of severe combined immunodeficiency.

9 April 2020

cites work

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Stem-cell gene therapy for the Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

An assessment of the effects of ectopic gp91phox expression in XCGD iPSC-derived neutrophils.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Cas9 as a versatile tool for engineering biology

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Multiplex genome engineering using CRISPR/Cas systems

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Genome editing in rice and wheat using the CRISPR/Cas system.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Genome editing. The new frontier of genome engineering with CRISPR-Cas9

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Targeted genome editing in human repopulating haematopoietic stem cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Residual NADPH oxidase and survival in chronic granulomatous disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Clinical manifestations of disease in X-linked carriers of chronic granulomatous disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

CRISPR-mediated genotypic and phenotypic correction of a chronic granulomatous disease mutation in human iPS cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Gene editing using ssODNs with engineered endonucleases.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Stable gene targeting in human cells using single-strand oligonucleotides with modified bases

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Use of internally nuclease-protected single-strand DNA oligonucleotides and silencing of the mismatch repair protein, MSH2, enhances the replication of corrected cells following gene editing

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Mobilization characteristics and strategies to improve hematopoietic progenitor cell mobilization and collection in patients with chronic granulomatous disease and severe combined immunodeficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Innate immunity against Granulibacter bethesdensis, an emerging gram-negative bacterial pathogen

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Humans with chronic granulomatous disease maintain humoral immunologic memory despite low frequencies of circulating memory B cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

AQP8 transports NOX2-generated H2O2 across the plasma membrane to promote signaling in B cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Dual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Biochemical correction of X-CGD by a novel chimeric promoter regulating high levels of transgene expression in myeloid cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

High-fidelity CRISPR-Cas9 nucleases with no detectable genome-wide off-target effects.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Broadening the targeting range of Staphylococcus aureus CRISPR-Cas9 by modifying PAM recognition

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

Engineered CRISPR-Cas9 nucleases with altered PAM specificities

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.AAH3480

10.1126/SCITRANSLMED.AAH3480

21 January 2018

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28077679%20AND%20SRC:MED&resulttype=core&format=json

9 April 2020

1 reference